Publications Library
Explore Sarepta’s library to find peer-reviewed publications by therapeutic area or program from 2018 onward.
The publications below are provided to support scientific exchange.
Publications may include information about investigational use(s) of compounds/products that
are not approved for use by the U.S. Food and Drug Administration (FDA) and/or are inconsistent
with the Prescribing Information. Sarepta does not recommend or suggest the use of any of its
products beyond the approved Prescribing Information.
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Estimating Utility Values Using the DMD-QoL: A Disease-Specific Preference-Based Measure for Duchenne Muscular Dystrophy (DMD)
Authors:
Bever A, Szabo SM, Jayasinghe P, Feeny D, Neumann PJ, Malone DC, Iannaccone ST, Gooch KL, Audhya IF
Journal:
Advances in Therapy
Published:
13 July 2026
The Effect of Early Initiation of Eteplirsen Treatment on the Cardiac and Motor Disease Course in an Individual with Duchenne Muscular Dystrophy
Authors:
Masalha Y, Zehavi Y, Musallam B, Khamaysi M, Abu Omer M, Fink DL, Spiegel R
Journal:
Frontiers in Pediatrics
Published:
09 July 2026
Cardiac Safety Outcomes in Delandistrogene Moxeparvovec Clinical Trials for Duchenne Muscular Dystrophy With up to 5Â Years of Follow-Up
Authors:
Veerapandiyan A, Bourke J, Soslow JH, Day JW, McDonald CM, Mendell JR, Zaidman CM, Mason S, Meng J, Vivien M, Murphy AP, Wandel C, Richardson J
Journal:
Cardiology and Therapy
Published:
01 July 2026
A Real-World Target Trial Emulation of Eteplirsen, Casimersen, and Golodirsen to Evaluate Survival Among Patients With Duchenne Muscular Dystrophy
Authors:
Dharmarajan S, Grabich S, Baxter R, Nadkar A, Schermer C
Journal:
Advances in Therapy
Published:
06 June 2026
Five-Year Outcomes With Delandistrogene Moxeparvovec in Patients With Duchenne Muscular Dystrophy: a Phase 1/2A Study
Authors:
Mendell JR, Sahenk Z, Lowes LP, Iammarino MA, Alfano LN, McDonald CM, Signorovitch JE, Jin J, Li J, Mason S, Rodino-Klapac LR
Journal:
Muscle and Nerve
Published:
03 June 2026
Advancements From the EVOLVE Study for Assessing Real-World Experience With Eteplirsen, Golodirsen, and Casimersen for the Treatment of DMD
Plain Language Summary
Authors:
Tian C, Grabich S, Veerapandiyan A, Scharf RJ, Santra S, Hornibrook S, Drummond K, Sehinovych I, Waldrop M
Journal:
Journal of Comparative Effectiveness Research
Published:
10 April 2026