Publications Library
Explore Sarepta’s library to find peer-reviewed publications by therapeutic area or program from 2018 onward.
The publications below are provided to support scientific exchange.
Publications may include information about investigational use(s) of compounds/products that
are not approved for use by the U.S. Food and Drug Administration (FDA) and/or are inconsistent
with the Prescribing Information. Sarepta does not recommend or suggest the use of any of its
products beyond the approved Prescribing Information.
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Cataloging Health State Utility Estimates for Duchenne Muscular Dystrophy and Related Conditions
Authors:
Do LA, Sedita LE, Klimchak AC, Salazar R, Kim DD
Journal:
Health and Quality of Life Outcomes
Published:
02 September 2024
Healthcare Stakeholder Perspectives on a Value Assessment Approach for Duchenne Muscular Dystrophy Therapies
Authors:
Fischer R, Furlong P, Kennedy A, Maynard K, Penrod M, Miller D, Laverty CG, Lowes LP, Kuntz NL, Shieh PB, Kondejewski J, Neumann PJ, Shafrin J, Willke RJ
Journal:
Journal of Multidisciplinary Healthcare
Published:
29 August 2024
Discriminatory Properties of the Quality-Adjusted Life Year Based Cost-Effectiveness Analyses for Patients With Disabilities: a Duchenne Muscular Dystrophy Case Study
Authors:
Klimchak AC, Sedita LE, Perfetto EM, Gooch KL, Malone DC
Journal:
Value in Health
Published:
31 July 2024
Current Challenges of Using Patient-Level Claims and Electronic Health Record Data for the Longitudinal Evaluation of Duchenne Muscular Dystrophy Outcomes
Plain Language Summary
Authors:
Gooch KL, Audhya I, Ricchetti-Masterson K, Szabo SM
Journal:
Advances in Therapy
Published:
30 July 2024
Quantifying the Insurance Value for Rare Diseases: Duchenne Muscular Dystrophy
Authors:
Shafrin J, Thahir S, Klimchak AC, Audhya I, Sedita LE, Romley JA
Journal:
The American Journal of Managed Care
Published:
10 July 2024
Eteplirsen Treatment for Duchenne Muscular Dystrophy: a Qualitative Patient Experience Study
Plain Language Summary
Authors:
Iff J, Carmichael C, McKee S, Sehinovych I, McNeill C, Tesi-Rocha C, Henricson E, Muntoni F, Kitchen H
Journal:
Advances in Therapy
Published:
03 July 2024