Publications Library
Explore Sarepta’s library to find peer-reviewed publications by therapeutic area or program from 2018 onward.
The publications below are provided to support scientific exchange.
Publications may include information about investigational use(s) of compounds/products that
are not approved for use by the U.S. Food and Drug Administration (FDA) and/or are inconsistent
with the Prescribing Information. Sarepta does not recommend or suggest the use of any of its
products beyond the approved Prescribing Information.
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Immune-Mediated Myositis Following Gene Therapy for Duchenne Muscular Dystrophy: a Case Report
Authors:
Iannaccone ST, Cai C, Rhem B, Batley K, Rajaram V, Greenberg BM, Dharia S, Zaidman CM
Journal:
Journal of Neurology
Published:
22 June 2024
Validity of Remote Live Stream Video Evaluation of the North Star Ambulatory Assessment in Patients With Duchenne Muscular Dystrophy
Authors:
Lowes LP, Alfano LN, Iammarino MA, Reash NF, Giblin K, Hu L, Yu L, Wang S, Salazar R, Mendell JR
Journal:
Public Library of Science (PLOS) ONE
Published:
16 May 2024
"You Take This Day by Day, Come What May": a Qualitative Study of the Psychosocial Impacts of Living With Duchenne Muscular Dystrophy
Authors:
Bever A, Audhya I, Szabo SM, Mickle A, Feeny D, Malone D, Neumann P, Iannaccone S, Gooch K
Journal:
Advances in Therapy
Published:
06 May 2024
Observing the Clinical Course of Duchenne Muscular Dystrophy in Medicaid Real-World Healthcare Data
Authors:
Qian C, Klimchak AC, Szabo SM, Popoff E, Iannaccone ST, Gooch KL
Journal:
Advances in Therapy
Published:
02 May 2024
Management of Select Adverse Events Following Delandistrogene Moxeparvovec Gene Therapy for Patients With Duchenne Muscular Dystrophy
Authors:
Zaidman CM, Goedeker NL, Aqul AA, Butterfield RJ, Connolly AM, Crystal RG, Godwin KE, Hor KN, Mathews KD, Proud CM, Kula Smyth E, Veerapandiyan A, Watkins PB, Mendell JR
Journal:
Journal of Neuromuscular Diseases
Published:
11 April 2024
Recombinant AAV Genome Size Effect on Viral Vector Production, Purification, and Thermostability
Graphical Abstract
Authors:
Ibreljic N, Draper BE, Lawton CW
Journal:
Molecular Therapy Methods & Clinical Development
Published:
14 March 2024