Publications Library
Explore Sarepta’s library to find peer-reviewed publications by therapeutic area or program from 2018 onward.
The publications below are provided to support scientific exchange.
Publications may include information about investigational use(s) of compounds/products that
are not approved for use by the U.S. Food and Drug Administration (FDA) and/or are inconsistent
with the Prescribing Information. Sarepta does not recommend or suggest the use of any of its
products beyond the approved Prescribing Information.
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Incidence of Kidney-Related Events in Patients With Duchenne Muscular Dystrophy: a Claims-Based Assessment
Plain Language Summary
Authors:
Spatola H, Drummond K, Logan J, Santra S, Grabich S
Journal:
Future Rare Diseases
Published:
16 March 2026
The Paradox of Life Extension Within Traditional Cost-Effectiveness Analysis: a Duchenne Muscular Dystrophy Case Study
Authors:
Sedita L, Klimchak A, Perfetto E, Gooch K, Malone DC
Journal:
Journal of Health Economics & Outcomes Research
Published:
18 February 2026
Learnings From Patient Mortality After Delandistrogene Moxeparvovec Administration: a Report of Two Cases and Expert Committee Considerations for Future Mitigation and Management
Authors:
Shieh PB, Proud C, Diamond T, Chapin CA, Ahmad J, Salama AD, Bönnemann CG, Soslow J, Byrne BJ, Veerapandiyan A, Brandsema JF, Matesanz S, Samelson-Jones BJ, Wilkins BJ, Gerber M, Godwin Wild KE, Mason S, Asher D, McDonald CM, Mendell JR
Journal:
Human Gene Therapy
Published:
12 February 2026
The Natural History of Becker Muscular Dystrophy: a Systematic Literature Review
Authors:
Mickle AT, Johnston KM, Ricchetti-Masterson KL, Kennedy AR, Korpach SGC, Gooch KL
Journal:
Journal of Neuromuscular Diseases
Published:
11 February 2026
Two-Year Outcomes Following Delandistrogene Moxeparvovec Treatment in Ambulatory Patients With Duchenne Muscular Dystrophy: Phase 3 EMBARK Trial
Authors:
Mendell JR, Muntoni F, McDonald CM, Mercuri EM, Ciafaloni E, Komaki H, Leon-Astudillo C, Nascimento A, Proud C, Schara-Schmidt U, Veerapandiyan A, Zaidman CM, Furgerson M, Ding K, Singh P, Potter R, Asher DR, Murphy AP, Reid C, Hooper G, Torre CO, Manfrini M, Rodino-Klapac LR
Journal:
Neurology and Therapy
Published:
10 January 2026
The Balancing Act of Paid Work and Caregiving in DMD: Results From a Cross-Section Survey
Authors:
Dunne JS, Szabo SM, Gooch KL, Morrison CL, Audhya IF
Journal:
Advances in Therapy
Published:
29 December 2025